European consensus for starting and stopping enzyme replacement therapy in adult patients with Pompe disease: a 10-year experience

Ans T. van der Ploeg, Michelle E. Kruijshaar, A. Toscano, Pascal Laforêt, C Angelini, R H Lachmann, S I Pascual Pascual, M Roberts, K Rösler, Thomas M. Stulnig, Pieter A. van Doorn, P Y K Van den Bergh, J Vissing, B Schoser, European Pompe Consortium