Delivery is key: lessons learnt from developing splice-switching antisense therapies

Caroline Godfrey, Lourdes R. Desviat, Bård Smedsrød, France Piétri-Rouxel, Michela A. Denti, Petra Disterer, Stéphanie Lorain, Gisela Nogales-Gadea, Valentina Sardone, Rayan Anwar, Samir El Andaloussi, Taavi Lehto, Bernard Khoo, Camilla Brolin, Willeke M.C. van Roon-Mom, Aurélie Goyenvalle, Annemieke Aartsma-Rus, Virginia Arechavala-Gomeza^*